FDA Approves First Cell-Based Gene Therapy, Becomes Most Expensive Drug In US
The U.S. Food and Drug Administration on Wednesday approved bluebird bio’s gene therapy for patients with a rare disorder requiring regular blood transfusions, and the drugmaker priced it at a record $2.8 million. The approval sent the company’s shares 8% higher and is for the treatment of beta-thalassemia, which causes Read more…






